Challenges of up-scaling lentivirus production and processing A McCarron, M Donnelley, C McIntyre, D Parsons Journal of biotechnology 240, 23-30, 2016 | 109 | 2016 |
Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral‐mediated gene transfer C McIntyre, S Byers, DS Anson The journal of gene medicine 12 (9), 717-728, 2010 | 49 | 2010 |
Lentiviral-mediated gene therapy for murine mucopolysaccharidosis type IIIA C McIntyre, ALD Roberts, E Ranieri, PR Clements, S Byers, DS Anson Molecular genetics and metabolism 93 (4), 411-418, 2008 | 45 | 2008 |
Large-scale production of lentiviral vectors using multilayer cell factories N Rout-Pitt, A McCarron, C McIntyre, D Parsons, M Donnelley Journal of Biological Methods 5 (2), 2018 | 37 | 2018 |
Skeletal response to lentiviral mediated gene therapy in a mouse model of MPS VII CE Macsai, ALK Derrick-Roberts, X Ding, KH Zarrinkalam, C McIntyre, ... Molecular Genetics and Metabolism 106 (2), 202-213, 2012 | 37 | 2012 |
Phenotypic characterization and comparison of cystic fibrosis rat models generated using CRISPR/Cas9 gene editing A McCarron, P Cmielewski, N Reyne, C McIntyre, J Finnie, F Craig, ... The American journal of pathology 190 (5), 977-993, 2020 | 35 | 2020 |
Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII J Bielicki, C McIntyre, DS Anson Molecular genetics and metabolism 101 (4), 370-382, 2010 | 32 | 2010 |
Correction of murine mucopolysaccharidosis type IIIA central nervous system pathology by intracerebroventricular lentiviral‐mediated gene delivery C McIntyre, ALK Derrick‐Roberts, S Byers, DS Anson The Journal of Gene Medicine 16 (11-12), 374-387, 2014 | 27 | 2014 |
Transient lentiviral vector production using a packed-bed bioreactor system A McCarron, M Donnelley, C McIntyre, D Parsons Human Gene Therapy Methods 30 (3), 93-101, 2019 | 26 | 2019 |
Lentiviral-mediated gene correction of mucopolysaccharidosis type IIIA DS Anson, C McIntyre, B Thomas, R Koldej, E Ranieri, A Roberts, ... Genetic Vaccines and Therapy 5, 1-8, 2007 | 25 | 2007 |
Role of basal cells in producing persistent lentivirus-mediated airway gene expression N Farrow, M Donnelley, P Cmielewski, E Roscioli, N Rout-Pitt, C McIntyre, ... Human Gene Therapy 29 (6), 653-662, 2018 | 23 | 2018 |
Transduction of ferret airway epithelia using a pre-treatment and lentiviral gene vector P Cmielewski, N Farrow, M Donnelley, C McIntyre, J Penny-Dimri, ... BMC pulmonary medicine 14, 1-7, 2014 | 21 | 2014 |
Correction of Methylmalonic Aciduria In Vivo Using a Codon-Optimized Lentiviral Vector ESY Wong, C McIntyre, HL Peters, E Ranieri, DS Anson, JM Fletcher Human Gene Therapy 25 (6), 529-538, 2014 | 21 | 2014 |
Therapies for neurological disease in the mucopolysaccharidoses D S Anson, C McIntyre, S Byers Current gene therapy 11 (2), 132-143, 2011 | 21 | 2011 |
Lobe-specific gene vector delivery to rat lungs using a miniature bronchoscope C McIntyre, M Donnelley, N Rout-Pitt, D Parsons Human Gene Therapy Methods 29 (5), 228-235, 2018 | 17 | 2018 |
Systemic scAAV9. U1a. hSGSH delivery corrects brain biochemistry in mucopolysaccharidosis type IIIA at early and later stages of disease JT Saville, ALK Derrick-Roberts, C McIntyre, M Fuller Human Gene Therapy 32 (7-8), 420-430, 2021 | 9 | 2021 |
Collection of cerebrospinal fluid from murine lateral ventricles for biomarker determination in mucopolysaccharidosis type IIIA C McIntyre, J Saville, M Fuller Journal of neuroscience methods 324, 108314, 2019 | 8 | 2019 |
Phenotypic characterization and comparison of Phe508del and cystic fibrosis transmembrane conductance regulator (CFTR) knockout rat models of cystic fibrosis generated by … A McCarron, P Cmielewski, N Reyne, C McIntyre, J Finnie, F Craig, ... Elsevier, 2020 | 2 | 2020 |
Transient Lentiviral Vector Production in HEK 293T Cells Using the BioFlo® 320 Control Station with a BioBLU® 5p Single-Use Packed-Bed Vessel A McCarron, M Donnelley, C McIntyre, D Parsons Application Note 2019, 0 | 2 | |
Update on the Australian cystic fibrosis rat colony D Parsons, P Cmielewski, A Mccarron, C Mcintyre, F Craig, J Finnie, ... Wiley, 2019 | 1 | 2019 |